Sign in

You're signed outSign in or to get full access.

PI

PepGen Inc. (PEPG)·Q1 2024 Earnings Summary

Executive Summary

  • PepGen reported Q1 2024 net loss of $18.0M and ended the quarter with $175.2M in cash, cash equivalents, and marketable securities, extending cash runway into 2026 following $86.3M net proceeds from equity offerings .
  • Clinical execution progressed: CONNECT1-EDO51 5 mg/kg cohort fully enrolled with preliminary safety, exon 51 skipping, and dystrophin data expected mid-2024; FREEDOM-DM1 preliminary data (≥5 mg/kg) expected in H2 2024 .
  • Regulatory momentum accelerated: MHRA authorized CONNECT2-EDO51 initiation in the U.K.; FDA granted Orphan Drug and Rare Pediatric Disease designations for PGN-EDO51 and Fast Track designation for PGN-EDODM1 .
  • No Q1 2024 earnings call transcript was available; comparisons to Wall Street consensus were not possible due to S&P Global data unavailability (attempted query returned error). Estimates context is noted as unavailable.

What Went Well and What Went Wrong

What Went Well

  • CONNECT1-EDO51 advanced with the 5 mg/kg cohort fully enrolled; preliminary safety, exon skipping, and dystrophin production readout remains on track for mid-2024 . “We are on track to achieve several significant milestones during the remainder of 2024, including sharing preliminary data from both the CONNECT1-EDO51 and FREEDOM-DM1 clinical trials” – James McArthur, Ph.D., President & CEO .
  • Regulatory tailwinds: MHRA authorized CONNECT2-EDO51 initiation (designed to support potential accelerated approval with CONNECT1 data), and FDA granted Orphan Drug and Rare Pediatric Disease designations for PGN-EDO51 and Fast Track for PGN-EDODM1 .
  • Strengthened balance sheet: $86.3M net proceeds in February and ATM activity lifted cash to $175.2M, extending runway into 2026, mitigating near-term financing risk .

What Went Wrong

  • Continued losses with no product revenue; net loss widened vs Q4 2023 context remains substantial at $18.0M, consistent with clinical-stage investment cycle (Q4 2023 net loss was $19.5M; Q3 2023 net loss was $23.3M) .
  • Operating expenses remain elevated to support clinical programs: R&D $14.7M (up slightly YoY); G&A $5.1M (higher YoY, consistent with prior commentary on personnel costs) . Prior management cited personnel-related costs as G&A drivers in FY23 .
  • Visibility remains event-driven; key efficacy readouts (dystrophin for EDO51, splicing/functional measures for EDODM1) are not yet reported, leaving execution and regulatory pathway assumptions to be validated later in 2024 .

Financial Results

MetricQ3 2023Q4 2023Q1 2024
Research and Development ($USD Millions)$20.540 $16.300 $14.732
General and Administrative ($USD Millions)$4.240 $4.511 $5.066
Total Operating Expenses ($USD Millions)$24.780 $20.811 $19.798
Operating Loss ($USD Millions)$(24.780) $(20.811) $(19.798)
Interest Income ($USD Millions)$1.578 $1.591 $1.735
Net Loss ($USD Millions)$(23.290) $(19.5) $(18.020)
Cash, Cash Equivalents and Marketable Securities ($USD Millions)$129.5 $110.4 $175.2
Shares Outstanding (Millions, quarter-end)23.8 23.8 32.4

Notes:

  • PepGen did not disclose EPS for Q1 2024 in the press release; Q3 2023 net loss per share was $(0.98) .
  • No revenue was disclosed in these press releases; company is clinical-stage with expense-driven P&L .

Guidance Changes

MetricPeriodPrevious GuidanceCurrent GuidanceChange
CONNECT1-EDO51 preliminary data (5 mg/kg: safety, exon 51 skipping, dystrophin)Mid-2024Preliminary data mid-2024 Preliminary data mid-2024 Maintained
CONNECT2-EDO51 initiation (U.K.; plan to extend to U.S. and other geographies)2024Initiation targeted Q1 2024 MHRA authorization to initiate; plans to extend to U.S./others subject to authorizations Updated detail (authorized; geographic plan reiterated)
FREEDOM-DM1 preliminary data (≥5 mg/kg)H2 2024Preliminary data H2 2024 Preliminary data H2 2024 Maintained
FREEDOM2-DM1 Phase 2 trialH2 2024Expected to open H2 2024 Initiation expected H2 2024 Maintained
Cash runwayThrough 2026Extended into 2026 with ~$80M offering Into 2026 with $86.3M net proceeds and total cash $175.2M Strengthened liquidity (maintained runway; larger cash)

Earnings Call Themes & Trends

TopicPrevious Mentions (Q-2 and Q-1)Current Period (Q1 2024)Trend
Dystrophin targets for EDO51Q-1 (Q4 2023 call): aiming >1% gain over background at 5 mg/kg; potential >9% at 10 mg/kg based on modeling and NHP/human single-dose skipping . Q-2 (Q3 2023 PR): proof-of-concept data mid-2024 .Preliminary data timing reaffirmed (mid-2024 for 5 mg/kg) .Consistent confidence; execution progressing.
DM1 splicing correction thresholds and functional readoutsQ-1: meaningful benefit expected with >25–60% splicing correction; functional measures include vHoT, strength, and mobility tests; single-dose could show splicing/myotonia changes . Q-2: hold lifted; target doses cleared; initial results in 2024 .Preliminary safety, splicing correction, and functional outcomes expected H2 2024 .On track; regulatory momentum (Fast Track) supports engagement .
Regulatory designationsQ-1: Fast Track for EDODM1 (detailed in Feb 2024 8-K) . Q-2: Orphan for EDODM1 .Orphan Drug and Rare Pediatric Disease for EDO51; MHRA authorization for CONNECT2 .Strengthening regulatory profile across programs.
R&D execution and study designQ-1: CONNECT1 5 mg/kg fully enrolled; CONNECT2 planned; FREEDOM1 dosed first patient; FREEDOM2 planned H2 2024 . Q-2: Trial site openings; dosing timeline .CONNECT1 enrollment confirmed; CONNECT2 authorized in U.K.; timelines reiterated .Advancing per plan.
Financing and runwayQ-1: ~$80M offering extends runway into 2026 . Q-2: runway into 2025 .$86.3M net proceeds; cash $175.2M; runway into 2026 .Improved liquidity profile.

Management Commentary

  • “Our team has made exceptional progress in the first quarter advancing multiple clinical trials for Duchenne muscular dystrophy (DMD) and myotonic dystrophy type 1 (DM1). We are on track to achieve several significant milestones during the remainder of 2024...” – James McArthur, Ph.D., President & CEO .
  • On EDO51 expectations: “At the 5 mg/kg dose level, we expect to see greater than 1% of normal levels of dystrophin protein above background... For our 10 mg/kg dose cohort... potentially achieve greater than 9% of normal levels of dystrophin protein” .
  • On EDODM1 mechanism and specificity: approach targets pathogenic CUG repeats to liberate MBNL1, correct splicing, and improve myotonia, aiming for disease-modifying effects .
  • On DM1 functional endpoints: vHoT myotonia assessments, strength tests, and mobility measures to correlate with splicing correction; single-dose may show splicing/myotonia changes with multiple doses needed for broader function .

Q&A Highlights

  • Dystrophin quantification approach: PepGen plans to report dystrophin above background; ≥1% net gain at 5 mg/kg would support confidence in achieving ≥9% at 10 mg/kg based on NHP and modeling .
  • Timeline and enrollment for 10 mg/kg: Investigator enthusiasm suggests timely recruitment; company will update when ready; cautious on committing exact timing .
  • DM1 endpoints and correlation: vHoT myotonia metric viewed as central; higher splicing correction (≥25–60%) correlates with meaningful myotonia and functional improvements in models .
  • Mechanism specificity for EDODM1: blocking pathogenic CUG repeats aims for specific correction with potential safety advantages vs indiscriminate DMPK knockdown .

Estimates Context

  • S&P Global consensus estimates for Q1 2024 (EPS, revenue) were unavailable at time of query due to a data access error, so comparison to Wall Street consensus could not be performed. As a clinical-stage company, PepGen did not disclose revenue and did not provide EPS in the Q1 2024 press release; net loss and operating expense details are provided above .

Key Takeaways for Investors

  • Near-term catalysts: CONNECT1-EDO51 5 mg/kg preliminary data mid-2024; FREEDOM-DM1 preliminary data in H2 2024 – both are potential stock-movers given management’s dystrophin (>1% at 5 mg/kg; potentially >9% at 10 mg/kg) and splicing/functional targets .
  • Regulatory positioning strengthened: MHRA authorization for CONNECT2-EDO51, FDA Orphan and Rare Pediatric Disease for EDO51, and Fast Track for EDODM1 enhance optionality for accelerated pathways and expedited interactions .
  • Liquidity de-risks execution: Cash $175.2M with runway into 2026 supports multiple readouts and trial initiation without near-term financing pressure; monitor disciplined OpEx as programs scale .
  • Watch dystrophin methodology and thresholds: Reporting “above background” is key; a ≥1% net gain at 5 mg/kg would support model assumptions for higher-dose cohorts; any deviation would impact the accelerated approval case .
  • For DM1, splicing and functional correlation is critical: vHoT and strength tests alongside splicing correction will frame clinical meaningfulness; >25–60% splicing correction aligns with robust myotonia improvement in models .
  • Absence of Q1 call transcript and unavailable Street estimates limits near-term “beat/miss” framing; focus shifts to clinical execution, regulatory milestones, and cash discipline .
  • Risk framework: Event-driven binary outcomes; enrollment, safety/tolerability, and regulatory feedback remain key variables as described in forward-looking statements and risk disclosures .

KPIs and Program Status

Program / KPIQ3 2023Q4 2023Q1 2024
CONNECT1-EDO51 statusDosing anticipated Q4 2023 or early Q1 2024; POC data mid-2024 5 mg/kg fully enrolled; preliminary data mid-2024 5 mg/kg fully enrolled; preliminary safety, exon skipping, dystrophin mid-2024
CONNECT2-EDO51 statusInitiation targeted Q1 2024 MHRA authorization referenced (March 2024) MHRA authorized CTA; plan to extend to U.S./others
FREEDOM-DM1 statusFDA lifted clinical hold; Health Canada CTA cleared; initial results 2024 First patient dosed (Dec 2023); prelim (≥5 mg/kg) H2 2024 Preliminary safety, splicing correction, functional outcomes H2 2024
Regulatory designationsOrphan for EDODM1 Fast Track for EDODM1 (Feb 2024) Orphan + Rare Pediatric for EDO51 (Mar 2024)
Cash runwayInto 2025 Into 2026 (~$80M offering) Into 2026 ($86.3M net proceeds; $175.2M cash)